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A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Non-Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-NTDT)

    • Agios Pharmaceuticals, Inc.
    • Burjeel Medical City
    • Dubai Thalassemia Center

    Project: Clinical Trial

    Project Details

    Description

    The primary purpose of this study is to compare the effect of mitapivat versus placebo on anemia in participants with alpha- or beta-non-transfusion dependent thalassemia (NTDT).

    Layman's description

    The mitapivat group will include approximately 114 participants. The placebo group will include approximately 57 participants.
    AcronymENERGIZE
    StatusActive
    Effective start/end date8/11/2131/12/28

    Collaborative partners

    Keywords

    • Anemia, Hemolytic, Congenital
    • Anemia, Hemolytic
    • Anemia
    • Hematologic Diseases
    • Hemoglobinopathies
    • Genetic Diseases, Inborn
    • Thalassemia
    • beta-Thalassemia
    • alpha-Thalassemia
    • Enzyme Activators
    • Molecular Mechanisms of Pharmacological Action
    • Mitapivat

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